BioMarin Pharmaceutical

BioMarin Pharmaceutical is a global biotechnology company that develops and commercializes innovative therapies for people living with rare and ultra-rare genetic diseases. The enterprise focuses on developing enzyme replacement therapies, small-molecule drugs, and pioneering gene therapies for conditions such as achondroplasia, phenylketonuria, and severe hemophilia A. Through molecular biology research and patient-focused drug development, BioMarin Pharmaceutical addresses debilitating genetic conditions.