Beam Therapeutics
Biotechnology & Life Sciences
Where
238 Main Street, Cambridge, MA, 02142
Overview
Beam Therapeutics is a biotechnology enterprise that pioneers base editing, an advanced form of CRISPR technology designed to make single-base transitions without double-stranded DNA breaks. The company engineers precision base editors that can correct, modify, or silence genetic sequences to treat hemoglobinopathies, sickle cell disease, and alpha-1 antitrypsin deficiency. By utilizing lipid nanoparticle delivery and mRNA architectures, Beam Therapeutics creates permanent genetic repairs with reduced genomic disruption.