Sarepta Therapeutics
Biotechnology & Life Sciences
Where
215 First Street, Cambridge, MA, 02142
Overview
Sarepta Therapeutics is a commercial-stage biopharmaceutical leader focused on developing precision genetic medicines for rare neuromuscular diseases. The company commercializes phosphorodiamidate morpholino oligomer therapies, including Exondys 51 and Vyondys 53, alongside the FDA-approved gene transfer therapy Elevidys for Duchenne muscular dystrophy. Through exon-skipping technologies and adeno-associated viral vectors, Sarepta Therapeutics improves motor function and lifespan for patients with rare genetic diseases.